Panayiota Trifillis Selected Research

ataluren

1/2022	Ataluren delays loss of ambulation and respiratory decline in nonsense mutation Duchenne muscular dystrophy patients.
12/2021	Meta-analyses of deflazacort versus prednisone/prednisolone in patients with nonsense mutation Duchenne muscular dystrophy.
10/2020	Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy.
1/2020	Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study.
10/2019	Ataluren use in patients with nonsense mutation Duchenne muscular dystrophy: patient demographics and characteristics from the STRIDE Registry.
11/2018	Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post HOC analysis from the ACT DMD trial.
5/2007	PTC124 targets genetic disorders caused by nonsense mutations.

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Panayiota Trifillis Research Topics

Disease

7	Duchenne Muscular Dystrophy (Muscular Dystrophy, Becker) 01/2022 - 01/2018
2	Disease Progression 01/2022 - 10/2020
1	Neoplasms (Cancer) 01/2016
1	Hypoxia (Hypoxemia) 01/2016
1	Cystic Fibrosis (Mucoviscidosis) 05/2007
1	Inborn Genetic Diseases (Disease, Hereditary) 05/2007
1	Azoospermia 02/2002

Drug/Important Bio-Agent (IBA)

8	Nonsense Codon (Nonsense Mutation)IBA 01/2022 - 05/2007
7	atalurenIBA 01/2022 - 05/2007
3	Proteins (Proteins, Gene)FDA Link 01/2016 - 02/2002
2	Pharmaceutical PreparationsIBA 01/2016 - 05/2007
2	Messenger RNA (mRNA)IBA 01/2016 - 02/2002
1	deflazacortIBA 12/2021
1	Prednisolone (Predate)FDA LinkGeneric 12/2021
1	Prednisone (Sone)FDA LinkGeneric 12/2021
1	CytokinesIBA 01/2016
1	3' Untranslated Regions (3' UTR)IBA 01/2016
1	Vascular Endothelial Growth Factor A (Vascular Endothelial Growth Factor)IBA 01/2016
1	RNA-Binding Proteins (RNA-Binding Protein)IBA 02/2002

Therapy/Procedure

1	Therapeutics 01/2016
1	Oral Administration 01/2016